The Professors' Posts

Rituximab and Leukine (GM-CSF)

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Terry Hamblin

My position on rituximab and G-CSF is like any scientist's should be. I have an open mind. My first reaction was that granulocytes take no part in ADCC and therefore there was no reason why G-CSF should work. GM-CSF seemed a better proposition, even though it is no longer available here in the UK. However, GM-CSF is more toxic and in real life it seemed to have very little difference in its clinical effect from G-CSF, which is why the Company has withdrawn it here.

We have an experimental anti-CD20 antibody here, that is being tried in various types of lymphoma. Before anybody asks, I should say that this is not an invitation to participate in clinical trials. We are not at that stage yet. In the test tube and in the guinea pig, this formulation is more active than Rituximab. But in our first few patient studies it has produced a very low white count, such that we needed to give G-CSF as support. Now, one of these patients who had failed rituximab went into a very good remission - lost her requirement for red cell transfusions and platelets rose dramatically. So I ask myself whether it was an interaction between the antibody and G-CSF.

I have been trying to see whether this is a possibility by asking and reading around. I asked, could granulocytes participate in ADCC? Although most scientists are think not, some think that they might have a minor role. Then I asked can G-CSF affect macrophage function? Again it seems that it might. It seems to be able to activate macrophages, though unlike GM-CSF it cannot make them proliferate.

The immune response cannot be neatly separated into components. The whole system is very complex, operating in a mixture of chemicals (cytokines, chemokines, integrins, addressins etc) that mediate the function of the cells involved. It had been thought that GM-CSF nudges the immune response in the direction of a TH1 response while G-CSF nudges it in the direction of TH2. Generally a TH1 response is favored by the pundits. However, these impressions all come from experiments in mice, which may not reflect the human situation. Even things like taking an ibuprofen tablet might change the polarity of the response.

There is also evidence that activation of granulocytes is necessary to kick-start the whole immune response (what used to be called a 'danger signal').

So in the end it all comes down to clinical experiment, which is why I am in favor of this study. If there is a consistent benefit in a large proportion of people using it, then undoubtedly the medical establishment will turn to it. There is a quote from Acts of the Apostles that is apposite, The Jewish teacher, Gamalial, said, "If their purpose or activity is of human origin, it will fail. But if it is from God, you will not be able to stop these men." (Acts 6 v 38). I'm not saying that there's anything Godlike about G-CSF, but if it works we will know, and if it doesn't work we'll know that too.

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